AinsiSera
AinsiSera t1_ixvnosp wrote
Reply to comment by Sariel007 in A novel medication for hemophilia B has just been approved by the Food and Drug Administration. The treatment is a form of gene therapy, intended to replace a dysfunctional gene that leaves people unable to control their bleeding. by Sariel007
I read elsewhere that those treatments easily add up to $100k/month, so honestly $3.5 mil is pretty cost effective competitively.
AinsiSera t1_izv42mz wrote
Reply to comment by aron65 in Base editing: Revolutionary therapy clears girl's incurable cancer by netsec_burn
In theory - this is a big step forward on targeted immunology. But I’m reading that what they did here was aim for a wipe out of her immune system, to be replaced by a new bone marrow transplant. Usually that can be accomplished by radiation but that didn’t work in this case.
It’s not applicable for other types of cancer yet because let’s say you have liver cancer - you wouldn’t want/need a tool that wipes out all liver cells.
That said, we’re at the cudgel stage with the technique. The ideas behind it and the tools developed will continue to advance, until we have a hammer, then a chisel, then a pen, then a micro laser.